Gene therapy has shown remarkable progress in treating various genetic diseases over the past few years. Its applications in treatment of the genetic disorders are extended beyond traditional therapies. These techniques are being explored as treatment of many genetic disorders including Duchenne muscular dystrophy, cystic fibrosis, Alzheimer’s disease, Parkinson’s disease, and Huntington disease.

In December 2023, the U.S. Food and Drug Administration approved two treatments,Casgevy and Lyfgenia, representing the first cell-based gene therapies for the treatmentof sickle cell disease (SCD) in patients 12 years and older.

When considering radiopharmaceutical therapies for cancer treatment, it is crucial for patients to engage in meaningful discussions with their healthcare teams. Asking the right questions can help understand what to expect during treatment.

Radiopharmaceutical therapy, or RPT, is emerging as a potential next wave in cancer treatment. Offering a precision approach to patient care, RPT allows physicians to deliver radioisotopes in a highly targeted way directly to tumors. The radioisotopes can be used either as a useful diagnostic tool, to help image the precise location of the tumors, or to kill cancer cells.